Table 2 Benefit score of the orphan drug benefit assessment processes
Data analysis | Number of events (n) | Percentage of overall data% | Number of events (n) | Percentage of overall data% |
|---|---|---|---|---|
Benefit score | Applied | Â | Granted | Â |
 Major | 45 | 56% | 10 | 12% |
 Considerable | 21 | 26% | 0 | 0% |
 Minor | 4 | 5% | 20 | 25% |
 Not quantifiable | 11 | 14% | 49 | 60% |
 No additional benefit | – | – | 2 | 2% |
Comparison | ||||
 Matching benefit scores | 15 | 19% | – | – |